Recruitment Strategies for Rare Disease & Niche Patient Populations: Building Patient-Centered Engagement to Improve Feasibility & Enrollment Success

• Partner with patient advocacy groups early to understand lived experience, shape protocol design, and develop recruitment and retention strategies that reflect community needs
• Balance scientific objectives with the patient voice to design trials that remain operationally feasible while reducing burden and improving long-term participation
• Explore real-world examples of creative patient engagement, from improving understanding of gene therapies to collaborating with advocacy organizations to address practical barriers beyond the reach of sponsors alone

Speakers:

Tara Hastings

Global Patient Engagement Lead, Rare Diseases, Rare Blood & Genomic Medicines

Sanofi